World Orphan Drug Congress USA started as a modest conference back in 2010, when the Rare Disease industry was beginning to boom. As the industry itself grew, as did the World Orphan Drug Congress. Now the industry is exploding and we are evolving once more to meet this demand.
To grow the breadth and scope of the event even further and embrace and empower rare disease advocacy like never before, this year we are launching Rare Disease Advocacy World. By bringing all of the stakeholders together at one event, you will have more opportunities to meet the people who can change your company’s bottom line, whilst the two separate conferences provide intimate settings allowing you to tailor your learning for your needs.
Main topics for 2015 include:
• Improving clinical development of orphan drugs
• Optimizing patient partnerships in rare disease
• Achieving regulatory approval
• Ensuring reimbursement
• Exploiting global trends and learning from recent successes
• Devising international strategies for improving orphan drug market access
• Improving manufacturing and distribution of orphan drugs
• Better orphan drug business models and commercialization strategies
• Helping patient groups understand the scientific mindset, characterize their disease and patients, develop a strategic plan, and learn to raise awareness and acquire funding through partners
2015 Speakers include:
• Ed Pezalla, VP, National Medical Director for Pharmacy Policy and Strategy, Aetna
• Jeff Meyers, President and Chief Executive Officer, Medicaid Health Plans of America (MHPA)
• Yi-Ou Wang, Founder and President, China Dolls Center for Rare Disorders
• Richard Moscicki, Deputy Center Director for Science Operations, Center for Drug Evaluation and Research, FDA
• Chander Seghal, Director, Common Drug Review (CDR) and Optimal Use of Drugs, CADTH
• Jim Sullivan, Director, Clinical Biomarkers, Vertex Pharmaceuticals
• Pat Furlong, President & CEO, Parent Project Muscular Dystrophy
• Megan O’Boyle, Chair, Registry and Repository Committee, Phelan-McDermit Syndrome
• Nick Sireau, Founder and Chief Executive Officer, AKU Society
• Nicole Boice, Founder and President, Global Genes